First Baby Receives Experimental Gene Therapy Directly Into Brain as Israeli Medical Team Reports Breakthrough
An eight-month-old baby has become the first known patient in the world to receive an experimental gene therapy delivered directly into the brain to treat a severe genetic disorder, according to Israeli health authorities.Read origin
The procedure was carried out at Schneider Children's Medical Center in collaboration with medical researchers, biotechnology experts and healthcare professionals.
Officials said the treatment was developed to target a rare and devastating inherited condition that affects brain function. The therapy was administered directly into the child's brain, marking a new step in the use of gene-based treatments for neurological disorders.
Sharing details of the development, Clalit Health Services described the procedure as the result of cooperation among Jewish and Arab Israeli doctors, scientists and innovators who worked together on the project.
“This treatment was made possible through the combined efforts of medical professionals, researchers and biotechnology experts,” the health providers said in a statement.
The organisations said the baby is the first person globally to receive this specific form of experimental gene therapy through direct brain delivery. Further monitoring and evaluation are expected as specialists assess the treatment's long-term effectiveness and safety.
The announcement has drawn attention from the international medical community as researchers continue exploring gene therapy as a potential option for treating rare genetic diseases.
Source: Clalit Health Services / Schneider Children's Medical Center Spokesperson's Office.